Variant: rs1057516403

present in Gene: SMPD1 present in Chromosome: 11 Position on Chromosome: 6394495 Alleles of this Variant: TT/-

rs1057516403 in SMPD1 gene and Niemann-Pick Disease, Type A PMID 14681755 2003 Niemann-Pick disease type A and B are clinically but also enzymatically heterogeneous: pitfall in the laboratory diagnosis of sphingomyelinase deficiency associated with the mutation Q292 K.

PMID 15877209 2005 Acid sphingomyelinase deficiency. Phenotype variability with prevalence of intermediate phenotype in a series of twenty-five Czech and Slovak patients. A multi-approach study.

PMID 18052040 2007 Carboxyl-terminal disulfide bond of acid sphingomyelinase is critical for its secretion and enzymatic function.

PMID 26499107 2016 SMPD1 Mutation Update: Database and Comprehensive Analysis of Published and Novel Variants.